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Neuronal ceroid lipofuscinosis
Apr 08, 2020
Polaryx Therapeutics Receives IND Approval From the FDA to Study PLX-200 Treatment for Patients With Juvenile Neuronal Ceroid Lipofuscinosis
Jan 29, 2020
REGENXBIO Announces Presentations at the 16th Annual WORLDSymposium(TM) 2020
Jan 20, 2020
Polaryx Therapeutics Receives IND Approval for PLX-200 From the FDA for the Treatment of Late Infantile Neuronal Ceroid Lipofuscinosis
Dec 23, 2019
Polaryx Therapeutics Submits Investigational New Drug Application to the U.S. FDA for the Treatment of Late Infantile Neuronal Ceroid Lipofuscinosis With PLX-200
Feb 07, 2019
BioMarin Announces Ongoing Study Demonstrates Durable Treatment Benefit from Brineura® (cerliponase alfa) for 3 Years
Nov 14, 2018
FDA Grants Orphan Drug Designation To RGX-181 Gene Therapy For The Treatment Of CLN2 Form Of Batten Disease
Aug 30, 2018
REGENXBIO Announces Pipeline Expansion with RGX-181 Gene Therapy for CLN2 Form of Batten Disease
Jun 09, 2018
Global Batten Community Unites To Launch Inaugural International Batten Disease (NCL) Awareness Day
Apr 24, 2018
New England Journal of Medicine Published Open-label Study Showing Brineura® (cerliponase alfa) Reduced the Rate of Clinical Decline of Children with CLN2 Disease, a Form of Batten Disease
Feb 26, 2018
Polaryx Therapeutics Received Orphan Drug Designation From the European Medicines Agency (EMA) for the Treatment of Neuronal Ceroid Lipofuscinosis With PLX-200
Feb 06, 2018
WORLDSymposium Recognizes BioMarin's Brineura® (cerliponase alfa) with 2018 New Treatment Award
Feb 05, 2018
BioMarin Announces 20 Presentations at 14th Annual WORLDSymposium(TM) 2018
Dec 11, 2017
Polaryx Therapeutics Receives Orphan Drug Designation From the US FDA for the Treatment of Neuronal Ceroid Lipofuscinoses With PLX-100
Oct 18, 2017
Popular Science Names BioMarin's Brineura® (cerliponase alfa) One of the Top Health Innovations of 2017 with "Best of What's New" Award
Aug 07, 2017
Polaryx Therapeutics Receives Orphan Drug Designation From the U.S. FDA for PLX-200 for Rare Pediatric Disease
Jun 01, 2017
European Commission Approves Brineura(TM) (cerliponase alfa), the First Treatment for CLN2 Disease, a Form of Batten Disease and Ultra-Rare Brain Disorder in Children
Latest News
May 5, 2024
California American Water celebrates Drinking Water Week and 50th anniversary of Safe Drinking Water Act
May 5, 2024
Paradise Greens Named #1 in Arizona for Artificial Grass Installation by Ranking Arizona 2024 Directory
May 5, 2024
BrainChip and Frontgrade Gaisler to Augment Space-Grade Microprocessors with AI Capabilities
May 5, 2024
Niger receives new Russian advisors, equipment
May 5, 2024
Top Afghan diplomat in India quits after $2m gold smuggling reports
May 5, 2024
Teijin Automotive Technologies Celebrates Opening of Huntington, Indiana, Facility Expansion
May 4, 2024
Berkshire Hathaway Inc. First Quarter 2024 Earnings Release
May 4, 2024
How to Prevent Heatstroke at Your Business with Airrex and PortaCool.
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Agenda
29
October
United Kingdom
Copthorne Tara Hotel, London, UK
International Dismounted Soldier, 29-30 October 2024, Copthorne Tara Hotel, London, UK
Navigating the Evolving Battlespace: Enhancing the Capabilities of the Dismounted Soldier The modern battlefield...
24
September
United Kingdom
Hilton London Syon Park, London, UK
Defence Transformation Conference, 24-26 September 2024, Hilton London Syon Park, London, UK
Returning for its 8th year, Defence Transformation 2024 will feature an updated format that will address all aspects of...
17
June
France
Parc des Expositions de Paris Nord Villepinte ZAC Paris Nord 2, 93420 Villepinte – France (Halls 5a – 5b – 6)
Eurosatory 2024, 17 - 21 June 2024, Parc des Expositions de Paris Nord Villepinte ZAC Paris Nord 2, 93420 Villepinte – France (Halls 5a – 5b – 6)
Eurosatory 2024 There can be no sustainable world without peace and security. Founded in 1967, the exhibition...
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