Jun 12, 2020
PTC Therapeutics Announces 2-year Data from Part 1 of SUNFISH and New Data from JEWELFISH Trials for Risdiplam in Patients with Spinal Muscular Atrophy
Nov 11, 2019
Risdiplam (RG7916) Pivotal SUNFISH Study Demonstrates Statistically Significant Improvement for Patients with Type 2/3 Spinal Muscular Atrophy
May 05, 2019
AveXis presented robust data at AAN demonstrating efficacy of Zolgensma® in broad spectrum of spinal muscular atrophy (SMA) patients
Oct 03, 2018
Risdiplam Demonstrates Preliminary Evidence of Clinical Benefit in Type 1, 2, & 3 Spinal Muscular Atrophy Patients
Jun 16, 2018
Updated Preliminary Data from SMA FIREFISH Program in Type 1 Babies Presented at the CureSMA Conference
Apr 27, 2018
Invitae Announces New Program to Offer Genetic Testing to Aid Diagnosis of Spinal Muscular Atrophy (SMA)
Apr 18, 2018
Preliminary Study Suggests Drug May Help Babies with Spinal Muscular Atrophy
Mar 15, 2018
FIREFISH Transitions into Pivotal Phase
Jan 27, 2018
Preliminary Data from FIREFISH trial in Type 1 SMA Infants Presented at the International Scientific Congress on Spinal Muscular Atrophy
Nov 16, 2017
Canon BioMedical launches assays for spinal muscular atrophy research
Oct 12, 2017
Spinal Muscular Atrophy Program Advances into Pivotal Study in SMA Patients
Oct 03, 2017
RG7916 Increased SMN Protein Production in SUNFISH Clinical Trial in Patients with Type 2/3 Spinal Muscular Atrophy
Jun 22, 2017
Spotlight Innovation to Present Poster at the Cure SMA 2017 Annual SMA Conference