Sep 05, 2019
Muscular Dystrophy Association Awards 25 Grants Totaling More Than $6.6 Million for Neuromuscular Disease Research
Aug 22, 2019
AskBio Applauds Pfizer's Continuing Investments in Gene Therapy
Aug 08, 2019
Parent Project Muscular Dystrophy Announces Children's Hospital of Richmond at VCU as Their 26th Certified Duchenne Care Center
Jul 16, 2019
MDA Awards Venture Philanthropy Funding to Dr. Rachelle Crosbie to Develop a Novel Membrane-Stabilizing Drug for Duchenne Muscular Dystrophy
Jul 02, 2019
AskBio's Perspective on Pfizer's 1b Clinical Trial Results on Duchenne MD Gene Therapy
Jun 28, 2019
PTC Provides Update on Translarna(TM) (ataluren) Application for Label Expansion
Jun 07, 2019
PTC Therapeutics Receives FDA Approval for the Expansion of the EMFLAZA® (deflazacort) Labeling to Include Patients 2-5 Years of Age
Jun 04, 2019
Parent Project Muscular Dystrophy Awards $175,000 Grant to UCLA to Explore Optimization of CRISPR Technology in Duchenne Muscular Dystrophy
May 30, 2019
Newly Approved Spinal Muscular Atrophy Gene Therapy, Zolgensma®, Validates AskBio Gene Therapy Platform
May 14, 2019
Muscular Dystrophy Association Awards 26 Grants Totaling More Than $7.5 Million for Neuromuscular Disease Research
May 07, 2019
Audentes Therapeutics Reports First Quarter 2019 Financial Results and Provides Corporate Update
Apr 29, 2019
Translarna(TM) (ataluren) is the First Therapy Approved in Brazil for Duchenne Muscular Dystrophy
Apr 18, 2019
Parent Project Muscular Dystrophy Awards $100,000 Grant to Nationwide Children's Hospital to Further Explore GALGT2 Gene Therapy in Duchenne Muscular Dystrophy
Apr 16, 2019
Muscular Dystrophy Association Convenes Regulatory, Clinical and Scientific Leaders to Showcase Latest Progress in the Field of Neuromuscular Disease
Apr 05, 2019
Dystrogen Therapeutics Announces That Gene Therapy Successfully Cuts Off Production of Neuron-Destroying Protein in Huntington's Disease
Mar 19, 2019
Cure SMA and Parent Project Muscular Dystrophy Announce Strategic Collaboration with Prometheus Research
Feb 11, 2019
Parent Project Muscular Dystrophy Designates University of Rochester Medical Center as a Certified Duchenne Care Center
Jan 31, 2019
PTC Therapeutics Launches New Program to Support Research Projects in Rare, Genetic Disorders
Jan 29, 2019
Parent Project Muscular Dystrophy Designates Children's Hospital of The King's Daughters as a Certified Duchenne Care Center
Jan 24, 2019
Parent Project Muscular Dystrophy Awards $105,000 Grant to University of Missouri to Explore a Mini-Dystrophin Gene Aimed at Protecting Cardiac Function