Jan 22, 2019
Global Emerging Gene Therapies 2019: CRISPR Patent Space, Emerging Regulatory Trends, Innovation Leaders and the Interests of Pharma in Gene Therapy
Dec 19, 2018
Parent Project Muscular Dystrophy Awards $329,000 Grant to Binghamton University to Examine the Role of the Immune System on Dystrophin Restoration
Nov 13, 2018
Evox Therapeutics Wins Funding From Duchenne UK to Explore Exosome-Mediated Delivery of Dystrophin
Nov 06, 2018
Parent Project Muscular Dystrophy Designates Children's Hospital of Wisconsin a Certified Duchenne Care Center
Nov 01, 2018
Parent Project Muscular Dystrophy Designates Children's National Health System, a Certified Duchenne Care Center
Oct 15, 2018
DMD Drugs Market Size Worth $4.11 Billion by 2023 | CAGR: 41.3%: Grand View Research, Inc.
Oct 06, 2018
PTC Therapeutics Announces Initial Data from Patient Registry Demonstrating Translarna(TM) (ataluren) Slows Disease Progression in Children with Duchenne Caused by a Nonsense Mutation
Sep 27, 2018
Miles for Matthew Marks 10-Year Anniversary
Sep 07, 2018
PTC Therapeutics Announces Winners of Global Duchenne Muscular Dystrophy Patient Group STRIVE Awards in Recognition of World Duchenne Awareness Day
Sep 07, 2018
Parent Project Muscular Dystrophy and Sarepta Therapeutics Partner to Launch Duchenne Outcomes Research Interchange, a Patient-Data Warehouse Serving the Entire Duchenne Community
Sep 06, 2018
Flagship's Digital Tissue Image Analysis Approach Validated in Assessment of Dystrophin Muscle Biopsies; Findings Published in Archives of Pathology & Laboratory Medicine
Sep 05, 2018
ARMGO Pharma Receives FDA Orphan Drug Designation for ARM210/S48168 for the Treatment of Ryanodine Receptor Type 1 Related Myopathies
Sep 05, 2018
Parent Project Muscular Dystrophy Designates American Family Children's Hospital, a Certified Duchenne Care Center
Aug 23, 2018
Muscular Dystrophy Association announces 34 new research grants totaling $9.9 million
Aug 02, 2018
First Patient Enrolled in Mallinckrodt's Phase 2 Duchenne Muscular Dystrophy Trial
Jul 24, 2018
PTC Therapeutics Announces Publication of Data Demonstrating the Clinical Differentiated Benefit of Deflazacort
Jul 09, 2018
PTC Therapeutics Announces Positive Data from its Translarna(TM) Phase II Clinical Trial in Children as Young as Two Years with Nonsense Mutation Duchenne Muscular Dystrophy
Jun 25, 2018
Decode Duchenne Announces 1,000th Patient Application
Jun 20, 2018
Biotech Resurgent Growth Championed by Cancer Research and Clinical Trial Advancements
May 07, 2018
Sarepta and Invitae Expand Partnership to Advance Clinical Research in Duchenne Muscular Dystrophy